NBDF showcases a wide array of findings from the latest in bleeding disorders research at our annual Bleeding Disorders Conference.

Anti-Gravity Treadmill Use in an Adult with Severe Hemophilic Arthropathy: A Case Report.
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Orthopedic and Physical Therapy

An analysis of fatalities in persons with congenital hemophilia A (PwcHA) reported in the FDA Adverse Event Reporting System (FAERS) database
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials

Evaluating BIVV001, a New Class of Factor VIII Replacement Therapy: A Phase 3 Study (XTEND-1) Design
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials

Characteristics of persons with hemophilia A treated with emicizumab with or without factor VIII inhibitors
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research

Non-severe hemophilia is not benign? - Insights from the PROBE Study
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research

Redefining Treatment Satisfaction and Its Impact on Treatment Adherence and Value for Persons with Hemophilia: Findings from the HemACTIVE Study
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research

Fear of pain in people with hemophilia and their families – a pilot study
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues

The Moti-VIII Study – Factors for Empowering Mobility and Well-being in Hemophilia A
AWARDED/PRESENTED: 2020
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research

Correcting Bleeding Disorders Using Blood Clotting Factors Produced in vivo by Encapsulated Engineered Allogeneic Human Cells
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Biomedical/Coagulation Research

Pain assessment and treatment in bleeding disorder care: The need for social work specific education
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues

AMT-061 (AAV5-Padua hFIX variant) an Enhanced Vector for Gene Transfer in Adults with Severe or Moderate-Severe Hemophilia B: Follow-up up to 9 Months in a Phase 2b trial
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials

Quality Improvement: An Initiative to Foster Mental Health Wellness among a Hemophilia Treatment Center Patient Population
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues

Baseline patient characteristics in ReITIrate: A prospective study of rescue ITI with recombinant factor VIII Fc fusion protein (rFVIIIFc) in patients who have failed previous ITI attempts
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials

Optimizing language for effective communication of gene therapy concepts: A qualitative study
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Peer Support/Outreach/Integration Models

Five-year safety and efficacy of N8-GP (ESPEROCT®) in previously treated children with hemophilia A in the completed pathfinder 5 trial
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials

Quality of life and health in patients with Haemophilia in Mexico
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research

Four-year safety and efficacy of N8-GP (ESPEROCT®) in previously treated adolescents/adults with hemophilia A in the completed pathfinder 2 trial
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials

Patients Report High Satisfaction with US Hemophilia Treatment Centers: National Trends 2014 and 2017
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research

Navigating the Emergency Department: A Collaboration Among Hemophilia Treatment Center Staff, Emergency Department Staff & Bleeding Disorder Chapter Staff
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Collaboration/Team Models

Patient Perspectives on the Impact of Severe or Moderate Hemophilia on Physical Activity: HemACTIVE Survey Findings from the US and Canada
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research