Stay informed with the latest updates for the inheritable blood disorders community.

Industry
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BioMarin to Narrow Its Commercial Focus for Hemophilia A Gene Therapy
Industry
Gene Therapy a pill with DNA
Pfizer Announces New Data from Hemophilia A Gene Therapy Study
Industry
FDA Approval Includes Full ALTUVIIIO™ Pediatric Trial Results
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Gene Therapy
Hemophilia B Gene Therapy Trial Data Published
Industry
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Takeda Announces Interim Trial Results for Investigational ITP Therapy
Industry
uniQure Announces Findings from HCC Case Investigation in HOPE-B Trial for Gene Therapy
Takeda's Voluntary Withdrawal: Alert on Misprinted Labels for VONVENDI®
Industry
FDA Accepts Biologics License Application for Marstacimab
Industry
CSL Presents Three Year Treatment Data for Hemophilia B Gene Therapy
Industry
FDA Grants Expanded Approval to Wilate® for Prophylaxis in All Types of…
Industry
First Patient Dosed with Hemophilia Gene Therapy Candidate ASC618
Industry
Sernova Receives Dual FDA Designations for Investigational Hemophilia…
Industry
Takeda Announces Trial Results on Investigational Therapy for Ultra Rare Blood Disorder
Investigational T-Cell Therapy for Hemophilia A…
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Clinical Trial Lab Research
New Trial Data Shows ALTUVIIIO™ Prophylaxis Effective in Children
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FDA Approval
Hemophilia A Gene Therapy Product Receives U.S. FDA Approval
Industry
First Hemophilia B Patient Dosed with Gene Therapy Product