Stay informed with the latest updates for the inheritable blood disorders community.

Industry
First Patient Dosed with Hemophilia Gene Therapy Candidate ASC618
Industry
Sernova Receives Dual FDA Designations for Investigational Hemophilia…
Industry
Takeda Announces Trial Results on Investigational Therapy for Ultra Rare Blood Disorder
Investigational T-Cell Therapy for Hemophilia A…
Industry
Clinical Trial Lab Research
New Trial Data Shows ALTUVIIIO™ Prophylaxis Effective in Children
Industry
FDA Approval
Hemophilia A Gene Therapy Product Receives U.S. FDA Approval
Industry
First Hemophilia B Patient Dosed with Gene Therapy Product
Industry
Research Blood Disorder Vial
Pfizer Highlights Phase 3 Trial Results of Marstacimab
Industry
Research Blood Disorder Vial
FDA Requests Additional Information on Concizumab from Novo Nordisk
Industry
Two Doctors/Researchers discussing data
Sanofi Announces Publication of Two Phase 3 Fitusiran Trials
Industry
Clinical Trial Gene Double Helix
BioMarin Announces FDA’s Extended Review of Investigational…
Industry
FDA Approval
uniQure Announces Published Trial Results for Approved Gene Therapy
Industry
FDA Approval
FDA Approves ALTUVIIIO™ for Hemophilia A Patients
Industry
Female Scientist Conducting Research in Lab Analyzing Data
Sanofi Announces New Efanesoctocog alfa Data Published in the NEJM
Industry
Scientist Pipetting Liquids for Research
New FIX Chromogenic Assay Launched by Precision BioLogic
Industry
Biomarin Provides Hemophilia A Clinical Development Program Updates
Biomarin Provides Hemophilia A Clinical Development Program Updates