Stay informed with the latest updates for the inheritable blood disorders community.

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Research Blood Disorder Vial
Pfizer Highlights Phase 3 Trial Results of Marstacimab
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Research Blood Disorder Vial
FDA Requests Additional Information on Concizumab from Novo Nordisk
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Two Doctors/Researchers discussing data
Sanofi Announces Publication of Two Phase 3 Fitusiran Trials
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Clinical Trial Gene Double Helix
BioMarin Announces FDA’s Extended Review of Investigational…
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FDA Approval
uniQure Announces Published Trial Results for Approved Gene Therapy
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FDA Approval
FDA Approves ALTUVIIIO™ for Hemophilia A Patients
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Female Scientist Conducting Research in Lab Analyzing Data
Sanofi Announces New Efanesoctocog alfa Data Published in the NEJM
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Scientist Pipetting Liquids for Research
New FIX Chromogenic Assay Launched by Precision BioLogic
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Biomarin Provides Hemophilia A Clinical Development Program Updates
Biomarin Provides Hemophilia A Clinical Development Program Updates
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Takeda Announces Trial Results on Investigational Therapy for Ultra Rare Blood Disorder
Takeda Announces Trial Results on Investigational Therapy for…
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Image of a blue gene helix with a red section in the center
Pfizer Announces Trial Updates for Investigational Hemophilia Gene Therapy…
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Clinical Trial Lab Research
Spark Announces SPK-8011 Updates at ASH
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BioMarin Shares Community Update for Valoctocogene Roxaparvovec
BioMarin Shares Community Update for Valoctocogene Roxaparvovec
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Clinical Trial Gene Therapy Double Helix
Recruitment Reopened for Phase 3 AFFINE Gene Therapy Trial
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Red Blood Cells
FDA Grants Priority Review for Sanofi’s BIVV001