Stay informed with the latest updates for the inheritable blood disorders community.

Industry
Doctor asking questions to patient about care
Rare Factor X Deficiency Survey Shows Disparity in Care
Industry
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BioMarin Receives Conditional Approval in Europe for Gene Therapy
Industry
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
Industry
New Prophylaxis Approval for REBINYN®
New Prophylaxis Approval for REBINYN®
Industry
Sanofi Provides Fitusiran Trial Updates at ISTH
Sanofi Provides Fitusiran Trial Updates at ISTH
Industry
Prophylactic Therapy for Glanzmann Thrombasthenia Moves Towards Clinical Trials
Prophylactic Therapy for Glanzmann Thrombasthenia Moves Towards…
Industry
Scientist using Microscope in a clinical trial
Sanofi and Sobi® Report Progress with BIVV001 at International Congress
Industry
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Bayer Announces Discontinuation of Kogenate® FS
Industry
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FDA Grants Breakthrough Status to BIVV001
Industry
DNA Gene Helix
FDA Accepts Priority Review BLA for Hemophilia B Gene Therapy
Industry
First Patient Dosed in Freeline’s Dose-Confirmation Trial for Hemophilia B Gene Therapy
First Patient Dosed in Freeline’s Dose-Confirmation Trial for…
Industry
BioMarin Provides Update Including Next Steps for Investigational Gene Therapy
BioMarin Provides Update Including Next Steps for Investigational Gene…
Industry
Sigilon Announces a Priority Shift in Light of Clinical Trial Setbacks
Sigilon Announces a Priority Shift in Light of Clinical Trial Setbacks
Industry
uniQure and CSL Behring Announce Trial Updates for Hemophilia B Gene…
Industry
Sigilon Reports Trial Updates for Investigational Hemophilia A Therapy