Stay informed with the latest updates for the inheritable blood disorders community.

Industry
Regulators Clear Roche Deal to Acquire Spark
Regulators Clear Roche Deal to Acquire Spark
Industry
Bayer Announces Data from Jivi Extension Study
Bayer Announces Data from Jivi Extension Study
Industry
Sangamo and Pfizer Announce Progress in Gene Therapy Trial at ASH
Sangamo and Pfizer Announce Progress in Gene Therapy Trial at ASH
Industry
UniQure Announces Interim Hemophilia B Gene Therapy Trial Data
UniQure Announces Interim Hemophilia B Gene Therapy Trial Data
Industry
UniQure Reaches Enrollment Goal in Phase 3 Gene Therapy Trial
UniQure Reaches Enrollment Goal in Phase 3 Gene Therapy Trial
Industry
Investigational Marstacimab Shows Promise in Laboratory Assays
Investigational Marstacimab Shows Promise in Laboratory Assays
Industry
Sigilon’s SIG-001 Receives Orphan Drug Designation
Sigilon’s SIG-001 Receives Orphan Drug Designation
Industry
New Lab Test Screens for Inhibitors in Patients Receiving Hemlibra®
New Lab Test Screens for Inhibitors in Patients Receiving Hemlibra®
Industry
Analysis Compares Prophylaxis with Emicizumab vs FVIII Replacement
Analysis Compares Prophylaxis with Emicizumab vs FVIII Replacement
Industry
Freeline Provides Updates on Hemophilia Gene Therapy Programs
Freeline Provides Updates on Hemophilia Gene Therapy Programs
Industry
Investigators Report Progress on New Subcutaneous Therapy
Investigators Report Progress on New Subcutaneous Therapy
Industry
Casebia Presents Dual Approach to Gene Therapy
Casebia Presents Dual Approach to Gene Therapy
Industry
BioMarin to Submit Marketing Applications to FDA and EMA
BioMarin to Submit Marketing Applications to FDA and EMA
Industry
Sanofi Presents Final Trial Data for rFVIII Candidate
Sanofi Presents Final Trial Data for rFVIII Candidate
Industry
uniQure Announces New Gene Therapy Trial Data
uniQure Announces New Gene Therapy Trial Data