Stay informed with the latest updates for the inheritable blood disorders community.

Medical
Person interacting with computer and taking notes
Virtual Grand Round Series to Focus on Hemophilia Gene Therapy
Industry
Red Blood Cells
FDA Grants Priority Review for Sanofi’s BIVV001
Industry
Doctor asking questions to patient about care
Rare Factor X Deficiency Survey Shows Disparity in Care
NBDF & Community
NHF Show Daily - Wrap-up Issue Monday August 29, 2022
Press Releases
bdc award winners 2022
NHF Announces its Awards of Excellence 2022 Winners
Industry
Gene Helix for Gene Therapy Image
BioMarin Receives Conditional Approval in Europe for Gene Therapy
Medical
NBDF and HFA Address Concerns on WHO's Recommendation of Cryoprecipitate
PPTA Posts Statement on Monkeypox and Plasma Protein Therapies
Industry
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
Industry
New Prophylaxis Approval for REBINYN®
New Prophylaxis Approval for REBINYN®
Peer-Reviewed Journal Summaries
Gene Therapy Helix
Paper Features Q&A Resource on Shared Decision Making and Gene Therapy
Industry
Sanofi Provides Fitusiran Trial Updates at ISTH
Sanofi Provides Fitusiran Trial Updates at ISTH
Industry
Prophylactic Therapy for Glanzmann Thrombasthenia Moves Towards Clinical Trials
Prophylactic Therapy for Glanzmann Thrombasthenia Moves Towards…
Industry
Scientist using Microscope in a clinical trial
Sanofi and Sobi® Report Progress with BIVV001 at International Congress
Advocacy & Legislative
NHF Addresses Potential Contraception Bans
NBDF & Community
NHF Employee Highlight - Meet Nick Kallinicou!