Stay informed with the latest updates for the inheritable blood disorders community.

Peer-Reviewed Journal Summaries
Prophylactic Therapy for Glanzmann Thrombasthenia Moves Towards Clinical Trials
Summit Emphasizes Pharmacovigilance in the Inherited Bleeding…
Industry
Clinical Trial Gene Double Helix
BioMarin Announces FDA’s Extended Review of Investigational…
NBDF & Community
Join the Conversation This #BleedingDisordersAwarenessMonth
Start the Conversation: Dr. Amy Dunn on Gene Therapy
NBDF & Community
Join the Conversation - #BleedingDisordersAwarenessMonth
Start the Conversation: Gene Therapy – An Oasis or Mirage?
Medical
Gene Helix for Gene Therapy Image
New Medscape Activity to Help Institutions Offer Gene Therapy
Press Releases
Pathway to Cures Research
Venture Philanthropy Fund to Accelerate the…
Press Releases
mike recht
National Hemophilia Foundation Names Michael…
Industry
FDA Approval
uniQure Announces Published Trial Results for Approved Gene Therapy
Advocacy & Legislative
Washington D.C. - Capitol Building
NHF Public Policy February Monthly Update
Industry
FDA Approval
FDA Approves ALTUVIIIO™ for Hemophilia A Patients
NBDF & Community
Una conversación sobre la equidad sanitaria con Anthony Llanes Rodríguez
Advocacy & Legislative
Takeda Announces Trial Results on Investigational Therapy for Ultra Rare Blood Disorder
APLUS Coalition Members Unite to Issue New Joint Statement
Peer-Reviewed Journal Summaries
Study Suggests Significant Rates of Depression and Anxiety for…
NBDF & Community
DEI - Artwork of Diverse Group of People Men Women
Kopenitz family commits substantial funding to NHF health equity…
Advocacy & Legislative
Additional Resources
Important Changes Coming to Your State Medicaid or CHIP Program