NBDF funds a broad range of research programs that seek to increase our understanding of the science behind bleeding disorders, how they affect people's lives, and pathways to better treatments and cures.

Studies of VWF Function in VWF-Platelet and VWF-FVIII Interactions

Studies of VWF Function in VWF-Platelet and VWF-FVIII Interactions

Year:
-
Grants:
Career Development Award
Von Willebrand Disease
Author(s):
Veronica Flood

Dr. Flood earned her undergraduate degree from Harvard University in 1995 and her doctorate from Tufts University in 1999. She is board certified in pediatrics as well as pediatric hematology/oncology. She has been serving as an Assistant Professor at the Medical College of Wisconsin, where she has been performing research and seeing patients since 2006.

As part of her NHF Career Development Award, Dr. Flood will study the common variants and interactions of the von Willebrand factor molecule as a means to enhance overall understanding and eventually improve upon current methods of von Willebrand disease testing. Using mouse models, she will investigate diagnostic alternatives by examining the interaction between ristocetin and its ability to bind to von Willebrand factor. As Dr. Flood states in her summary, "Improved testing for VWD will prevent patients with normal VWF function from receiving unnecessary treatment, while allowing more accurate assessment of patients with true defects in VWD."

Regulatory Mechanisms in the Activation of Blood Coagulation Factors V and VIII

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Factor V
Hemophilia A (Factor VIII/F8)
Author(s):
Mettine Bos

Pharmacogenomics of Hemophilia Therapy: Genetics of Inhibitor Antibody Response

Year:
-
Grants:
Career Development Award
Inhibitors
Author(s):
Jay Lozier
Qizen Shi

Immune Response in Platelet-Derived FVIII Gene Therapy of Murine Hemophilia A

Year:
-
Grants:
Career Development Award
Gene Therapy
Hemophilia A (Factor VIII/F8)
Platelets
Author(s):
Qizhen Shi

Targeting Dendritic Cells to Induce Immune Tolerance to Factor VIII

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Hemophilia A (Factor VIII/F8)
Inhibitors
Author(s):
Ruijin Su

Recombinant Factor VIIa and RL Platelets as a Hemophilia Therapy

Year:
-
Grants:
Career Development Award
Platelets
Hemophilia A (Factor VIII/F8)
Hemophilia B (Factor IX/F9)
Factor VII/F7
Author(s):
Alisa Wolberg

Proficient AAV Vectors for the Treatment of Hemophilia B (2007)

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Hemophilia B (Factor IX/F9)
Gene Therapy
Author(s):
Jyoti Mathur
Junjiang_Sun

Hemophilic Arthropathy: Gene Delivery Vectors for Determining Mechanisms and Therapy

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Gene Therapy
Hemophilic Arthropathy
Pain
Author(s):
Jun-Jiang Sun

Self-Regulating HIV Vectors for Hemophilia A Gene Therapy

Year:
-
Grants:
Career Development Award
Gene Therapy
HIV/AIDS
Hemophilia A (Factor VIII/F8)
Author(s):
Yashuhiro Ikeda

Illinois Amish Community Outreach Project

Year:
-
Grants:
Social Work Excellence Fellowship
Author(s):
Jenny Purdy
Our goal is to establish an outreach clinic in an area that will serve the Amish bleeding disorder community. After the completion of our formal project, we plan to continue to offer our services to the community to provide ongoing education, screening, and testing for individuals with bleeding symptoms or with a family history of a bleeding disorder. Furthermore, we plan to extend our clinical support to the other Amish communities located in downstate Illinois.

A Disease-Specific DNA Chip for von Willebrand Disease

Year:
-
Grants:
Career Development Award
Von Willebrand Disease
Author(s):
Bradley E. Aouizerat

Platelets as Modifiers of Phenotype in Hemophilia A

Year:
-
Grants:
Career Development Award
Hemophilia A (Factor VIII/F8)
Platelets
Author(s):
Donald L. Yee

Proficient AAV Vectors for the Treatment of Hemophilia B (2005)

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Hemophilia B (Factor IX/F9)
Gene Therapy
Author(s):
Michael Herbert

Transposon Mediated Gene Therapy of Hemophilia

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Gene Therapy
Hemophilia A (Factor VIII/F8)
Hemophilia B (Factor IX/F9)
Author(s):
Li Liu

Identification of Chemical Modifiers of Coagulation

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Hemophilia A (Factor VIII/F8)
Hemophilia B (Factor IX/F9)
Author(s):
David Buchner

Regulation of Factor V and VIII Secretion by an ER to Golgi Transport Receptor

Year:
-
Grants:
Career Development Award
Factor V
Hemophilia A (Factor VIII/F8)
Author(s):
Bin Zhang
Christine_Kempton

Platelet Mechanism Regulating Thrombin Generation

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Platelets
Author(s):
Christine L. Kempton

Per Dr. Kempton, the JGP assisted her in determining the direction of her future research. As a result of her JGP project, Dr. Kempton was published in ATVB and published several abstracts.

Depletion of Immune Response to AAV-F.IX

Year:
-
Grants:
Career Development Award
Hemophilia B (Factor IX/F9)
Gene Therapy
Author(s):
Huang-Ge Zhang

Purification and Characterization of Vitamin K Epoxide Reductase

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Vitamin K
Author(s):
Tao Li

Development of Self-Complimentary (SC) Adeno-Associated Virus Type 5 (AAV-5) Vectors for Gene Therapy of Hemophilia B

Year:
-
Grants:
Judith Graham Pool Postdoctoral Research Fellowship
Gene Therapy
Hemophilia B (Factor IX/F9)
Author(s):
Zhijian Wu